Author Correction: Myocardial reprogramming by HMGN1 underlies heart defects in trisomy 21

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一场罕见病攻坚2021年,德国Georg Schett教授团队首次使用抗CD19 CAR-T成功治疗了一位难治性系统性红斑狼疮患者,这一里程碑事件如同投入湖面的石子,激起了整个行业的巨大涟漪。

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